Three Philadelphia scientists won a $3 million Breakthrough Prize for developing the first FDA-approved gene therapy for a genetic disease, prize sponsors announced Saturday. Their work created a ...
Two Philadelphia doctors who led the groundbreaking gene-editing treatment of baby boy from Delaware County are included ...
Pfizer announced in February 2025 that it was taking Beqvez (fidanacogene elaparvovec), its gene therapy for hemophilia B, ...
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
Morning Overview on MSN
First human trial tests gene therapy aimed at reversing cellular aging
For the roughly 80 million people worldwide living with glaucoma, daily life often means watching the world slowly close in.
J&J will hand over the rights to bota-vec for $25 million upfront, clearing MeiraGTx to seek regulatory approvals in the U.S.
Pfizer and BioMarin have pulled their hemophilia gene therapies, citing low demand. To prepare for his presentation at the ...
The new method relies on methyl groups, small chemical tags attached to DNA that regulate whether genes are on or off. This ...
Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.
Roche is launching a new global phase 3 trial for the controversial Duchenne muscular dystrophy gene therapy Elevidys in ...
Sarepta Therapeutics Inc.'s bid for the full Federal Circuit’s review of a revived gene-therapy patent dispute with RegenxBio ...
The Breakthrough Prize Foundation awarded researchers involved in developing gene therapies for blindness and sickle cell ...
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