The investigational gene therapy SGT-003 is showing early signs of safety and efficacy for Duchenne muscular dystrophy in a ...

This time, her baby did test positive for SMA type 1, a severe neurodegenerative genetic condition that typically results in ...

Keros Therapeutics will use the Massachusetts General Hospital MyMatch program to design a clinical trial testing rinvatercept for ALS.

NEW YORK (AP) — Anaheim Ducks defenseman Radko Gudas has been suspended five games for his knee-on-knee hit that injured Toronto Maple Leafs captain Auston Matthews and sidelined him for the rest of ...

“Yes, doctor. My dad’s first fall was on his 65th birthday. He stood in the driveway and suddenly dropped backwards on his back. After he fell two more times, we came to the clinic.” The symptoms the ...

This week's biotech landscape witnessed key FDA approvals, EU approvals, IND clearances, acquisitions, and clinical trial data readouts across key therapeutic areas such ...

Revised 3.2. Measurement of TC, LDL-C, HDL-C, TG, and Non–HDL-C COR 2a: For adults with an LDL-C level <70 mg/dL (<1.8 mmol/L), measurement of direct LDL-C or modified LDL-C estimate is reasonable to ...