A new method for safely inserting large chunks of DNA into genomes has now measured up in mice, potentially paving the way ...
Gene editing, a set of techniques used to alter sections of an organism's DNA, is helping scientists cure diseases previously ...
The U.S. Food and Drug Administration approved the first cell-based gene therapies for sickle cell disease, including the ...
A 19-year-old Canadian man becomes the first human cured through prime gene editing after doctors corrected a rare genetic ...
After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...
INSTALL results showed successful and safe non-viral insertion of large genetic payloads in the livers of mice when delivered by lipid nanoparticles (LNPs). In contrast, mice experienced fatal immune ...
Prime Medicine's application will test an FDA that has promised to speed new gene-editing treatments but has recently spurned ...
Drug delivery researchers have vastly improved the potential of genetic therapies by overcoming the challenge of consistently getting genes and gene-editing tools where they need to be within cells.
A version of this Priestley Medal address will be presented at the American Chemical Society Spring 2026 meeting ...
One year after receiving CRISPR gene editing therapy at CHOP, a Delaware County baby is thriving, and doctors want to expand treatment to others.
A study has traced thousands of conserved regulatory elements back 300 million years, revealing deep principles of plant ...
Gene therapy has long promised to provide a solution for genetic blood disorders, but delivering on that promise has proven complex due to challenges including difficulties delivering the editing ...